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Alagille Syndrome

Catch-up height, weight seen after maralixibat treatment in patients with ALGS

Patients with Alagille syndrome (ALGS) treated with the ileal bile acid transporter inhibitor (IBATi), maralixibat, experienced catch-up height and weight, with the greatest catch-up in height observed in those with the greatest height disadvantage at baseline, according to a presentation at ESPGHAN 2022. Data from 34 participants from 3 clinical...

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